Pharmaxis initiates phase III trial in lung disease
Bronchiectasis is an incurable, degenerative and chronic inflammatory condition of the lungs affecting more than half a million people worldwide. The trial, which will investigate the safety and
ReviR Therapeutics has received a rare paediatric disease designation (RPDD) from the US Food and Drug Administration (FDA) for RTX-117, its investigational oral small-molecule therapy for Charcot-Marie-Tooth disease (CMT).