GSK, Amicus in fabry disease drug Amigal development pact
Migalastat HCl is an investigational treatment for fabry disease and has the potential to be the first in a new class of oral, small molecule medicines called pharmacological
miRecule has signed a research collaboration with EM subsidiary Rio Biofarma Brasil (RBBL) to co-develop peptide-mediated delivery technologies aimed at improving targeted ribonucleic acid (RNA) therapeutics delivery to tissues beyond the liver and muscles in a range of disease areas.