Human Genome says cancer drug is safe
“Preclinical studies have shown that adding HGS-ETR1 to gemcitabine and cisplatin results in increased cytotoxicity. These data warrant further study of HGS-ETR1 in combination with chemotherapeutic agents in
Ultragenyx Pharmaceutical has received accelerated approval from the US Food and Drug Administration (FDA) for its gene therapy, Genglycos (pariglasgene brecaparvovec-opnr), to treat glycogen storage disease type Ia (GSDIa).