CHMP awards positive opinion for myelodysplastic syndrome drug
The Committee for Medicinal Products for Human Use’s (CHMP’s) positive opinion is based on data from the AZA-001 trial, which has demonstrated an overall survival benefit for higher-risk
Ionis Pharmaceuticals has entered a licence agreement granting global pharmaceutical company Recordati exclusive rights to develop and commercialise zilganersen to treat Alexander disease (AxD) in countries outside the US.
The randomized, placebo-controlled, third-party double-blind, dose escalating Phase I clinical trial will study Protexia administered intramuscularly at one and two time points in healthy human volunteers. Approximately 32